标题:Editing Aberrant Splice Sites with Cas9 and Cas12a Efficiently Restores beta-Globin Expression in beta-Thalassemia
作者:Luk, Kevin; Xu, Shuqian; Yao, Qiuming; Shen, Anne H.; Zeng, Jing; Wu, Yuxuan; Luo, Hong-Yuan; Brendel, Christian; Pinello, Luca; Chu 更多
作者机构:[Luk, Kevin; Wolfe, Scot A.] Univ Massachusetts, Sch Med, Worcester, MA USA.; [Xu, Shuqian; Yao, Qiuming; Shen, Anne H.; Zeng, Jing; Wu, Yuxuan; Bre 更多
会议名称:22nd Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT)
会议日期:APR 29-MAY 02, 2019
来源:MOLECULAR THERAPY
出版年:2019
卷:27
期:4
页码:447-448
收录类别:CPCI-S;SCIE
资源类型:会议论文
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